Usher syndrome is a group of inherited disorders characterised by a combination of sensorineural hearing loss and retinitis pigmentosa.

Usher syndrome is a group of inherited disorders characterised by a combination of hearing loss and visual impairment due to retinitis pigmentosa.

RNA is involved in protein production from DNA in human cells. Mutations in DNA can be passed down to RNA, and a non-functional protein might be produced. RNA therapies target these "mistakes" in the RNA so that a normal functional protein can be produced instead.